Bone marrow burden score is not useful as a follow-up parameter in stable patients with type 1 Gaucher disease after 5  years of treatment

CONCLUSIONS: The BMB score is useful for response monitoring in the first five years of treatment. We recommend that, after 5 years of treatment, MRI for BMB evaluation should only be performed in non-adherent patients or in those who develop symptoms of acute skeletal disease.PMID:34242856 | DOI:10.1016/j.bcmd.2021.102591

Source: Blood Cells, Molecules and Diseases - July 9, 2021 Category: Hematology Authors: Livia d' Ávila Paskulin Rodrigo Tzovenos Starosta D ébora Bertholdo Filippo Pinto Vairo Leonardo Vedolin Ida Vanessa Doederlein Schwartz Source Type: research