Generation of transgene-free iPSC lines from three patients with Friedreich’s ataxia (FRDA) carrying GAA triplet expansions in the first intron of FXN gene

Publication date: Available online 27 June 2021Source: Stem Cell ResearchAuthor(s): Simge Kelekçi, Deniz Uğurlu-Çimen, Deniz Ata, Burcu Özçimen, Abdullah Burak Yıldız, Mehmet Batuhan Karakuş, Esra Börklü Yücel, Tamer T. Önder
Source: Stem Cell Research - Category: Stem Cells Source Type: research