Gene Transfer Study of ABO-102 in Patients With Middle and Advanced Phases of MPS IIIA Disease

Conditions:   MPS IIIA;   Sanfilippo Syndrome;   Sanfilippo A;   Mucopolysaccharidosis III Intervention:   Drug: ABO-102 Sponsor:   Abeona Therapeutics, Inc Not yet recruiting
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials
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