Gene Transfer Study of ABO-102 in Patients With Middle and Advanced Phases of MPS IIIA Disease
Conditions: MPS IIIA; Sanfilippo Syndrome; Sanfilippo A; Mucopolysaccharidosis III Intervention: Drug: ABO-102 Sponsor: Abeona Therapeutics, Inc Not yet recruiting
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials