Lentiviral-mediated Gene Therapy of Fanconi Anemia Patients Subtype A

Condition:   Fanconi Anemia Interventions:   Procedure: IV administration of Genetically Engineered Hematopoietic Stem/Progenitors Cells (HSPCs);   Biological: Genetically Engineered Hematopoietic Stem/Progenitor Cells;   Other: Laboratory Biomarker Analysis;   Biological: Filgrastim;   Drug: Plerixafor;   Procedure: Bone Marro w Aspiration Sponsors:   Hospital Infantil Universitario Niño Jesús, Madrid, Spain;   Centro de Investigaciones Energéticas, Medioambientales y Tecnológicas (CIEMAT);   Centro de Investigación en Red de Enfermedades Raras (CIBERER);   Instituto de Investigación Sanitaria de la Fundación Jiménez Díaz;   Hosp ital Vall d'Hebron;   Universitat Autonoma de Barcelona Recruiting - verified May 2017
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials