New step towards the treatment of myotubular myopathy gene therapy restores strength and prolongs lives in affected dogs

(AFM-T é l é thon) A team of researchers in France demonstrated the efficacy of administration of a therapeutic vector by a single intravenous injection and identified the dose that restores long-term muscular strength in a large animal model of the disease.
Source: EurekAlert! - Medicine and Health - Category: Global & Universal Source Type: news