Groundbreaking gene therapy offers ‘glimmer of hope’ for children with rare diseases

Within the first few weeks after Lori and Lee Greenwood ’s daughter Noa was born, her parents knew that something was wrong. A lot of different things, actually. The infant cried inconsolably. She wouldn’t follow her parents with her eyes, leading to concerns about her vision. She struggled to gain weight and missed milestone after milestone. She was slow to even respond to her parents’ presence. After weeks and months of having doctors dismiss it as the normal fits and fuss of a newborn, the…
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