Advancing rare disease treatment: EMA’s decade-long insights into engineered adoptive cell therapy for rare cancers and orphan designation
Gene Therapy, Published online: 14 March 2024; doi:10.1038/s41434-024-00446-0Advancing rare disease treatment: EMA’s decade-long insights into engineered adoptive cell therapy for rare cancers and orphan designation
Source: Gene Therapy - Category: Genetics & Stem Cells Authors: Maria Elisabeth Kalland Tomas Pose-Boirazian Gloria Maria Palomo Frauke Naumann-Winter Enrico Costa Darius Matusevicius Dinah M. Duarte Eva Malikova Dinko Vitezic Kristina Larsson Armando Magrelli Violeta Stoyanova-Beninska Segundo Mariz Source Type: research