SA60 Key Challenges in Gene Therapy Development for Usher Syndrome: Insights from Machine-Assisted Rapid Scoping Review

Despite proven potential through empirical evidence, gene therapies for Usher syndrome (USH) are not approved yet. This scoping review aimed to systematically evaluate the challenges reported in the existing literature on USH gene therapy.

Source: Value in Health - December 1, 2023 Category: International Medicine & Public Health Authors: R. Bhat, B. Nallamothu, F. Shethia, V. Chhaya, K. Khambholja Source Type: research