A Study to Investigate the Efficacy and Safety of OTL-203 in Subjects With MPS-IH Compared With Standard of Care With Allogeneic HSCT

Conditions: MPS-IH (Hurler Syndrome) Interventions: Genetic: Experimental: OTL-203; Genetic: Active Comparator: Allo-HSCT Sponsors: Orchard Therapeutics Not yet recruiting
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials
More News: Genetics | Research | Study