Measurement properties of the EQ-5D-5L and PROPr in patients with spinal muscular atrophy

Spinal muscular atrophy (SMA) is a rare monogenic neuromuscular disorder caused by loss of function mutations. Measuring health-related quality of life to support economic evaluations in this population is enc...

Source: Health and Quality of Life Outcomes - November 15, 2023 Category: International Medicine & Public Health Authors: Richard Huan Xu, Bin Ma, Huanping Xin, Huanyu Zhang, Yan Zeng, Nan Luo and Dong Dong Tags: Research Source Type: research