Gene Therapy Promising for Rare Jaundice Syndrome

(MedPage Today) -- Gene therapy for Crigler-Najjar syndrome appeared promising in patients treated at a higher dose, a phase I/II trial showed. A single infusion of GNT0003 -- an adeno-associated virus serotype 8 vector carrying a correction...
Source: MedPage Today Gastroenterology - Category: Gastroenterology Source Type: news