First gene therapy for deadly form of muscular dystrophy gets FDA approval for young children

The first gene therapy for a deadly form of muscular dystrophy received preliminary U.S. approval on Thursday despite concerns from some government scientists about the treatment’s ability to help boys with the inherited disease. The Food and Drug Administration approval provides a new option for…#fda #sareptatherapeutics #iv #petermarks #lougehrigs #duchenne #cambridge #massachusetts #sarepta #pfizer
Source: Reuters: Health - Category: Consumer Health News Source Type: news