19 The inflammation in the pathology of patients with mucopolysaccharidosis

Conclusions These results provide the rational for individual treatment trials (ITTs) with the aim to evaluate immunomodulatory molecules, repurposed in MPS. Furthermore, they will – together with the results of the ITTs – be utilized for the development of a decision tool for the personalized treatment of unmet clinical needs in these patients.
Source: Archives of Disease in Childhood - Category: Pediatrics Authors: Tags: General abstracts Source Type: research