Microdystrophin Expression as a Surrogate Endpoint for Duchenne Muscular Dystrophy Clinical Trials

Human Gene Therapy, Ahead of Print.

https://www.liebertpub.com/doi/abs/10.1089/hum.2022.190?ai=s5&mi=o0fy&af=R

Source: Human Gene Therapy - March 14, 2023 Category: Genetics & Stem Cells Authors: Jeffrey S. Chamberlain Melissa Robb Serge Braun Kristy J. Brown Olivier Danos Annie Ganot Pedro Gonzalez-Alegre Nina Hunter Craig McDonald Carl Morris Mark Tobolowsky Kathryn R. Wagner Olivia Ziolkowski Dongsheng Duan Source Type: research

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