Clinical Study of UX701 AAV-Mediated Gene Transfer for the Treatment of Wilson Disease
Condition:   Wilson Disease Interventions:   Genetic: UX701;   Other: Placebo;   Drug: oral corticosteroids;   Drug: Placebo for oral corticosteroids Sponsor:   Ultragenyx Pharmaceutical Inc Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 13, 2021 Category: Research Source Type: clinical trials

Copper and Molybdenum Balance in Participants With Wilson Disease Treated With ALXN1840
Condition:   Wilson Disease Intervention:   Drug: ALXN1840 Sponsor:   Alexion Pharmaceuticals Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 2, 2020 Category: Research Source Type: clinical trials