A Natural History Study of Molybdenum Cofactor and Isolated Sulfite Oxidase Deficiencies
Conditions: Molybdenum Cofactor Deficiency; Isolated Sulfite Oxidase DeficiencyIntervention: Sponsor: Alexion PharmaceuticalsRecruiting - verified January 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 26, 2012 Category: Research Source Type: clinical trials
A Retrospective, Observational, Noninterventional Data Collection Study for Patients With Molybdenum Cofactor Deficiency Who Have Been Previously Treated With Cyclic Pyranopterin Monophosphate (cPMP)
Condition: Molybdenum Cofactor DeficiencyIntervention: Sponsor: Alexion PharmaceuticalsRecruiting - verified October 2014 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - July 13, 2012 Category: Research Source Type: clinical trials