Friedreich's Ataxia Clinical Trials This is an RSS file. You can use it to subscribe to this data in your favourite RSS reader or to display this data on your own website or blog.
Study to Evaluate Multiple Ascending Dose and Multi-Dose of DT-216 in Adult Patients With Friedreich Ataxia
Condition: Friedreich Ataxia Interventions: Drug: DT-216; Drug: Placebo Sponsor: Design Therapeutics Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 10, 2022 Category: Research Source Type: clinical trials
A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich Ataxia
Condition: Friedreich Ataxia Intervention: Drug: Vatiquinone Sponsor: PTC Therapeutics Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 25, 2022 Category: Research Source Type: clinical trials