Study to Evaluate Multiple Ascending Dose and Multi-Dose of DT-216 in Adult Patients With Friedreich Ataxia
Condition:   Friedreich Ataxia Interventions:   Drug: DT-216;   Drug: Placebo Sponsor:   Design Therapeutics Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 10, 2022 Category: Research Source Type: clinical trials

A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich Ataxia
Condition:   Friedreich Ataxia Intervention:   Drug: Vatiquinone Sponsor:   PTC Therapeutics Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 25, 2022 Category: Research Source Type: clinical trials