Global Safety and Efficacy Registration Study of Crinecerfont in Pediatric Patients With Classic Congenital Adrenal Hyperplasia (CAHtalyst Pediatric Study)
Condition:   Congenital Adrenal Hyperplasia Interventions:   Drug: Crinecerfont;   Drug: Placebo Sponsor:   Neurocrine Biosciences Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 19, 2021 Category: Research Source Type: clinical trials

A Study of Gene Therapy for Classic Congenital Adrenal Hyperplasia (CAH)
Condition:   Congenital Adrenal Hyperplasia Intervention:   Biological: BBP-631 Sponsor:   Adrenas Therapeutics Inc Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 5, 2021 Category: Research Source Type: clinical trials