HALOS: A Safety, Tolerability, Pharmacokinetics and Pharmacodynamics Study of Multiple Ascending Doses of ION582 in Participants With Angelman Syndrome
Condition:   Angelman Syndrome Intervention:   Drug: ION582 Sponsor:   Ionis Pharmaceuticals, Inc. Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 19, 2021 Category: Research Source Type: clinical trials

Angelman Syndrome Natural History Study- FAST UK
Condition:   Angelman Syndrome Intervention:   Other: Natural History Study Sponsors:   University of Oxford;   Foundation for Angelman Syndrome Therapeutics UK;   Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 29, 2021 Category: Research Source Type: clinical trials