HALOS: A Safety, Tolerability, Pharmacokinetics and Pharmacodynamics Study of Multiple Ascending Doses of ION582 in Participants With Angelman Syndrome
Condition: Angelman Syndrome Intervention: Drug: ION582 Sponsor: Ionis Pharmaceuticals, Inc. Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 19, 2021 Category: Research Source Type: clinical trials
Angelman Syndrome Natural History Study- FAST UK
Condition: Angelman Syndrome Intervention: Other: Natural History Study Sponsors: University of Oxford; Foundation for Angelman Syndrome Therapeutics UK; Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 29, 2021 Category: Research Source Type: clinical trials