Angelman Syndrome Video Assessment (ASVA) Source Material Study
Condition: Angelman Syndrome Intervention: Sponsors: The Emmes Company, LLC; Ionis Pharmaceuticals, Inc.; Boston Children's Hospital Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 5, 2022 Category: Research Source Type: clinical trials
Study to Investigate the Pharmacokinetics and Safety and to Provide Proof of Mechanism of Alogabat in Children and Adolescents Aged 5-17 Years With Angelman Syndrome (AS) With Deletion Genotype
Condition: Angelman Syndrome Interventions: Drug: 60 mg QD Alogabat; Drug: 40 mg QD Alogabat; Drug: 7 mg QD Alogabat; Drug: Part 2 Adult Alogabat High Dose (aged 15-17); Drug: Alogabat; Drug: Aligabat Sponsor: Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 29, 2022 Category: Research Source Type: clinical trials