Angelman Syndrome Video Assessment (ASVA) Source Material Study
Condition:   Angelman Syndrome Intervention:   Sponsors:   The Emmes Company, LLC;   Ionis Pharmaceuticals, Inc.;   Boston Children's Hospital Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 5, 2022 Category: Research Source Type: clinical trials

Study to Investigate the Pharmacokinetics and Safety and to Provide Proof of Mechanism of Alogabat in Children and Adolescents Aged 5-17 Years With Angelman Syndrome (AS) With Deletion Genotype
Condition:   Angelman Syndrome Interventions:   Drug: 60 mg QD Alogabat;   Drug: 40 mg QD Alogabat;   Drug: 7 mg QD Alogabat;   Drug: Part 2 Adult Alogabat High Dose (aged 15-17);   Drug: Alogabat;   Drug: Aligabat Sponsor:   Hoffmann-La Roche Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 29, 2022 Category: Research Source Type: clinical trials