Evaluation of the dystrophin carboxy-terminal domain for micro-dystrophin gene therapy in cardiac and skeletal muscles in the DMDmdx rat model

Gene Therapy, Published online: 01 February 2022; doi:10.1038/s41434-022-00317-6Evaluation of the dystrophin carboxy-terminal domain for micro-dystrophin gene therapy in cardiac and skeletal muscles in the DMDmdx rat model

Source: Gene Therapy - February 1, 2022 Category: Genetics & Stem Cells Authors: Audrey Bourdon Virginie Fran çois Liwen Zhang Aude Lafoux Bodvael Fraysse Gilles Toumaniantz Thibaut Larcher Tiphaine Girard Mireille Ledevin Cyrielle Lebreton Agn ès Hivonnait Anna Creismeas Marine Allais Basile Marie Justine Guguin V éronique Blouin Source Type: research