Restoration of RPGR expression in vivo using CRISPR/Cas9 gene editing

Gene Therapy, Published online: 14 July 2021; doi:10.1038/s41434-021-00258-6Restoration of RPGR expression in vivo using CRISPR/Cas9 gene editing
Source: Gene Therapy - Category: Genetics & Stem Cells Authors: Source Type: research
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