Sirolimus can Increase the Disappearance Rate of Cardiac Rhabdomyomas Associated with Tuberous Sclerosis: A Prospective Cohort and Self-controlled Case Series Study

To investigate the efficacy and safety of sirolimus in the treatment of cardiac rhabdomyomas ) associated with tuberous sclerosis complex (TSC) and the specific benefits in different subgroups.

Source: The Journal of Pediatrics - February 22, 2021 Category: Pediatrics Authors: Xiao-Qiao Chen, Yang-Yang Wang, Meng-Na Zhang, Qian Lu, Ling-Yu Pang, Li-Ying Liu, Yu-Fen Li, Li-Ping Zou Tags: Original Articles Source Type: research