Development of a dual hybrid AAV vector for endothelial-targeted expression of von Willebrand factor
Gene Therapy, Published online: 17 January 2021; doi:10.1038/s41434-020-00218-6Development of a dual hybrid AAV vector for endothelial-targeted expression of von Willebrand factor
Source: Gene Therapy - Category: Genetics & Stem Cells Authors: Elena Barbon Charlotte Kawecki Solenne Marmier Aboud Sakkal Fanny Collaud Severine Charles Giuseppe Ronzitti Caterina Casari Olivier D. Christophe C écile V. Denis Peter J. Lenting Federico Mingozzi Source Type: research