UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
Conditions: Adrenoleukodystrophy; Batten Disease; Mucopolysaccharidosis II; Leukodystrophy, Globoid Cell; Leukodystrophy, Metachromatic; Neimann Pick Disease; Pelizaeus-Merzbacher Disease; Sandhoff Disease; Tay-Sachs Disease; Brain Diseases, Metabolic, InbornIntervention: Biological: DUOC-01Sponsors: Joanne Kurtzberg, MD; Marcus Foundation; Duke UniversityRecruiting - verified October 2014
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials