UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells

Conditions:   Adrenoleukodystrophy;   Batten Disease;   Mucopolysaccharidosis II;   Leukodystrophy, Globoid Cell;   Leukodystrophy, Metachromatic;   Neimann Pick Disease;   Pelizaeus-Merzbacher Disease;   Sandhoff Disease;   Tay-Sachs Disease;   Brain Diseases, Metabolic, InbornIntervention:   Biological: DUOC-01Sponsors:   Joanne Kurtzberg, MD;   Marcus Foundation;   Duke UniversityRecruiting - verified October 2014
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials