Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant
New England Journal of Medicine,Volume 377, Issue 23, Page 2215-2227, December 2017.
Source: New England Journal of Medicine - Category: Internal Medicine Authors: Lindsey A. George Spencer K. Sullivan Adam Giermasz John E.J. Rasko Benjamin J. Samelson-Jones Jonathan Ducore Adam Cuker Lisa M. Sullivan Suvankar Majumdar Jerome Teitel Catherine E. McGuinn Margaret V. Ragni Alvin Y. Luk Daniel Hui J. Fraser Wright Yife Source Type: research