Study to Evaluate the Safety and Efficacy of Ace-ER Tablets in Patients With GNE Myopathy or Hereditary Inclusion Body Myopathy

Conditions:   Hereditary Inclusion Body Myopathy;   Distal Myopathy With Rimmed Vacuoles;   Distal Myopathy, Nonaka Type;   GNE Myopathy;   Quadriceps Sparing MyopathyIntervention:   Drug: Aceneuramic Acid Extended-Release TabletsSponsor:   Ultragenyx Pharmaceutical IncEnrolling by invitation - verified April 2016
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials