Study to Evaluate the Safety and Efficacy of Ace-ER Tablets in Patients With GNE Myopathy or Hereditary Inclusion Body Myopathy
Conditions: Hereditary Inclusion Body Myopathy; Distal Myopathy With Rimmed Vacuoles; Distal Myopathy, Nonaka Type; GNE Myopathy; Quadriceps Sparing MyopathyIntervention: Drug: Aceneuramic Acid Extended-Release TabletsSponsor: Ultragenyx Pharmaceutical IncEnrolling by invitation - verified April 2016
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials