Prospective, Longitudinal Study of the Natural History and Functional Status of Patients With Myotubular Myopathy (MTM)
Condition: Myotubular MyopathyIntervention: Sponsors: Valerion Therapeutics, LLC; Institut de Myologie, France; GenethonRecruiting - verified February 2014
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials