Voretigene neparvovec for inherited retinal dystrophy due to RPE65 mutations: a scoping review of eligibility and treatment challenges from clinical trials to real practice

Eye, Published online: 16 April 2024; doi:10.1038/s41433-024-03065-6Voretigene neparvovec for inherited retinal dystrophy due to RPE65 mutations: a scoping review of eligibility and treatment challenges from clinical trials to real practice

Source: Eye - April 16, 2024 Category: Opthalmology Authors: Francesco Testa Giacomo Bacci Benedetto Falsini Giancarlo Iarossi Paolo Melillo Dario Pasquale Mucciolo Vittoria Murro Anna Paola Salvetti Andrea Sodi Giovanni Staurenghi Francesca Simonelli Source Type: research