Utilizing real-world evidence to investigate treatments in alternating hemiplegia of childhood: Implications for future trials in rare disease

Eur J Paediatr Neurol. 2024 Apr 6:S1090-3798(24)00040-0. doi: 10.1016/j.ejpn.2024.04.002. Online ahead of print.NO ABSTRACTPMID:38600015 | DOI:10.1016/j.ejpn.2024.04.002
Source: European Journal of Paediatric Neurology - Category: Neurology Authors: Source Type: research