First Gene Therapy for Children With Metachromatic Leukodystrophy Approved by FDA

FRIDAY, March 22, 2024 -- The U.S. Food and Drug Administration has approved Lenmeldy (atidarsagene autotemcel) as the first gene therapy for the treatment of children with metachromatic leukodystrophy (MLD). Lenmeldy is a one-time, individualized...
Source: Drugs.com - Pharma News - Category: Pharmaceuticals Source Type: news