Patient-reported impact of symptoms in adrenoleukodystrophy (PRISM-ALD)

Adrenoleukodystrophy (ALD) is a multifaceted, X-linked, neurodegenerative disorder that comprises several clinical phenotypes. ALD affects patients through a variety of physical, emotional, social, and other d...

Source: Orphanet Journal of Rare Diseases - March 19, 2024 Category: Internal Medicine Authors: Anika Varma, Jennifer Weinstein, Jamison Seabury, Spencer Rosero, Nuran Dilek, John Heatwole, Charlotte Engebrecht, Shaweta Khosa, Kaitlin Chung, Asif Paker, Amy Woo, Gregory Brooks, Chan Beals, Rohan Gandhi and Chad Heatwole Tags: Research Source Type: research