Therapeutic Strategy for Fabry Disease by Intravenous Administration of Adeno-Associated Virus 9 in a Symptomatic Mouse Model
Human Gene Therapy,Volume 35, Issue 5-6, Page 192-201, March 2024.
Source: Human Gene Therapy - Category: Genetics & Stem Cells Authors: Yuka Hayashi Yoshihide Sehara Ryota Watano Kenji Ohba Yuki Takayanagi Yoshio Sakiyama Kazuhiro Muramatsu Hiroaki Mizukami Source Type: research