FDA approves Orchard ’s gene therapy for children with rare genetic disease

This decision marks the first FDA-approved treatment for children with a rare genetic disease called metachromatic leukodystrophy (MLD) and Orchard's entry into the U.S. drug market.

Source: bizjournals.com Health Care:Pharmaceuticals headlines - March 18, 2024 Category: Pharmaceuticals Authors: Hannah Green Source Type: news