A Delphi panel to build consensus on assessing disease severity and disease progression in adult patients with hypophosphatasia in the United States

ConclusionsThese statements regarding disease severity, progression, and assessment methods address some knowledge gaps in adult patients with HPP and may be helpful for treating HCPs, although the small sample size affects the ability to generalize the healthcare provider experience.
Source: Journal of Endocrinological Investigation - Category: Endocrinology Source Type: research