What is gene therapy, and how does it work?

The Food and Drug Administration on Thursday approved a treatment that uses gene therapy to treat severe hemophilia A, a rare and sometimes fatal blood disorder. The new drug, Roctavian, could save people with the severe form of the disease from a lifetime of frequent injections. The drug’s maker…#roctavian #hemophilia #fda #hemgenix
Source: Reuters: Health - Category: Consumer Health News Source Type: news