Review of cardiac safety in onasemnogene abeparvovec gene replacement therapy: translation from preclinical to clinical findings

Gene Therapy, Published online: 25 April 2023; doi:10.1038/s41434-023-00401-5Review of cardiac safety in onasemnogene abeparvovec gene replacement therapy: translation from preclinical to clinical findings

Source: Gene Therapy - April 25, 2023 Category: Genetics & Stem Cells Authors: Deepa H. Chand Rui Sun Karim A. Diab Damien Kenny Francis Fonyuy Tukov Source Type: research