rAAV-mediated over-expression of acid ceramidase prevents retinopathy in a mouse model of Farber lipogranulomatosis

Gene Therapy, Published online: 28 July 2022; doi:10.1038/s41434-022-00359-wrAAV-mediated over-expression of acid ceramidase prevents retinopathy in a mouse model of Farber lipogranulomatosis

Source: Gene Therapy - July 28, 2022 Category: Genetics & Stem Cells Authors: Hanmeng Zhang Murtaza S. Nagree Haoyuan Liu Xiaoqing Pan Jeffrey A. Medin Daniel M. Lipinski Source Type: research