Study of Modified Atkins Diet in Kabuki Syndrome
Condition: Kabuki Syndrome Intervention: Dietary Supplement: Modified Atkins diet Sponsor: Hugo W. Moser Research Institute at Kennedy Krieger, Inc. Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 25, 2021 Category: Research Source Type: clinical trials
Exploiting Epigenome Editing in Kabuki Syndrome: a New Route Towards Gene Therapy for Rare Genetic Disorders
Condition: Kabuki Syndrome 1 Intervention: Genetic: Intervention on primary cultured cells Sponsors: University Hospital, Montpellier; Association Française contre les Myopathies Telethon Active, not recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 27, 2019 Category: Research Source Type: clinical trials