Study of Modified Atkins Diet in Kabuki Syndrome
Condition:   Kabuki Syndrome Intervention:   Dietary Supplement: Modified Atkins diet Sponsor:   Hugo W. Moser Research Institute at Kennedy Krieger, Inc. Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 25, 2021 Category: Research Source Type: clinical trials

Exploiting Epigenome Editing in Kabuki Syndrome: a New Route Towards Gene Therapy for Rare Genetic Disorders
Condition:   Kabuki Syndrome 1 Intervention:   Genetic: Intervention on primary cultured cells Sponsors:   University Hospital, Montpellier;   Association Française contre les Myopathies Telethon Active, not recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 27, 2019 Category: Research Source Type: clinical trials