Magnetic Resonance Imaging and Ultrasound Comparison With Load Evaluation
Conditions: Muscular Dystrophy, Facioscapulohumeral Interventions: Diagnostic Test: Muscle ultrasound with surface electromyography and dynamometry; Diagnostic Test: MRI scan Sponsors: Radboud University Medical Center; Solve FSHD Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 26, 2024 Category: Research Source Type: clinical trials

A Bicentric, Randomized, Double Blind, Placebo-controlled Pilot Study to Evaluate the Efficacy and Safety of Satralizumab in FSHD1
Conditions: Facioscapulohumeral Muscular Dystrophy 1 Interventions: Drug: Satralizumab Prefilled Syringe; Drug: Placebo Comparator Sponsors: Centre Hospitalier Universitaire de Nice Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 25, 2024 Category: Research Source Type: clinical trials

Study of ARO-DUX4 in Adult Patients With Facioscapulohumeral Muscular Dystrophy Type 1
Conditions: Facio-Scapulo-Humeral Dystrophy Interventions: Drug: ARO-DUX4 for Injection; Drug: Placebo Sponsors: Arrowhead Pharmaceuticals Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 15, 2023 Category: Research Source Type: clinical trials

Unraveling Metabolic Involvement in Facioscapulohumeral Dystrophy Through Metabolomics
Conditions: Facioscapulohumeral Muscular Dystrophy Interventions: Other: metabolomic on plasma sample Sponsors: University Hospital, Angers; University of Modena and Reggio Emilia; Federico II University Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 17, 2023 Category: Research Source Type: clinical trials

An 18-month Prospective Natural History Study to Gain Insight Into FSHD2 Pathophysiology and Disease Progression
Conditions: Facioscapulohumeral Muscular Dystrophy Type 2 Interventions: Diagnostic Test: Validation of new COMs for FSHD2 patients Sponsors: Centre Hospitalier Universitaire de Nice Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 12, 2023 Category: Research Source Type: clinical trials

New Biomarkers in Facioscapulohumeral Muscular Dystrophy, Multispectral Optoacoustic Tomography.
Condition:   FSHD Intervention:   Device: MSOT Acuity Echo Sponsor:   Fondazione Policlinico Universitario Agostino Gemelli IRCCS Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 15, 2023 Category: Research Source Type: clinical trials