Natural History Study for Achromatopsia
Condition:   Achromatopsia Intervention:   Diagnostic Test: Ocular assessments Sponsor:   MeiraGTx UK II Ltd Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 11, 2019 Category: Research Source Type: clinical trials

PBA Use for Treatment of ATF6-/- Patients
Conditions:   ACHROMATOPSIA 7;   Achromatopsia Intervention:   Drug: PBA Sponsor:   Columbia University Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 1, 2019 Category: Research Source Type: clinical trials