Allele-Specific Knockdown of Mutant Huntingtin Protein via Editing at Coding Region Single Nucleotide Polymorphism Heterozygosities

Human Gene Therapy,Volume 33, Issue 1-2, Page 25-36, January 2022.

Source: Human Gene Therapy - January 17, 2022 Category: Genetics & Stem Cells Authors: Sarah R. Oikemus Edith L. Pfister Ellen Sapp Kathryn O. Chase Lori A. Kennington Edward Hudgens Rachael Miller Lihua Julie Zhu Akanksh Chaudhary Eric O. Mick Miguel Sena-Esteves Scot A. Wolfe Marian DiFiglia Neil Aronin Michael H. Brodsky Source Type: research