Pegvaliase for the treatment of phenylketonuria: Results of the phase 2 dose-finding studies with long-term follow-up

Publication date: Available online 16 June 2020Source: Molecular Genetics and MetabolismAuthor(s): Barbara K. Burton, Nicola Longo, Jerry Vockley, Dorothy K. Grange, Cary O. Harding, Celeste Decker, Mingjin Li, Kelly Lau, Orli Rosen, Kevin Larimore, Janet Thomas, on behalf of the PAL-002 and PAL-004 Investigators
Source: Molecular Genetics and Metabolism - Category: Genetics & Stem Cells Source Type: research