Novel Gene ‐Editing Technique Cures β‐Thalassemia in Utero: A novel peptide nucleic acid‐based gene–editing technique using a nanoparticle delivery system seemingly cured beta thalassemia in fetal mice

American Journal of Medical Genetics Part A,Volume 176, Issue 10, Page 2052-2053, October 2018.
Source: American Journal of Medical Genetics Part A - Category: Genetics & Stem Cells Source Type: research