Potentially Protective Agent Shows Benefit in Niemann-Pick Type C

(MedPage Today) -- Patients with Niemann-Pick disease type C who received N-acetyl-L-leucine (NALL), an agent that potentially ameliorates lysosomal and metabolic dysfunction, showed reduced neurologic signs and symptoms after 3 months, a phase...
Source: MedPage Today Neurology - Category: Neurology Source Type: news