CO67 Development of an Investigator Global Assessment of Severity in Propionic Acidemia

To develop an Investigator Global Assessment of Severity (IGA-S) in propionic acidemia (PA).

Source: Value in Health - December 1, 2023 Category: International Medicine & Public Health Authors: N. Longo, V. Sikirica, S. Grunewald, O. Moshkovich, C. Dionisi-Vici, J. Vockley, M.A. Bellenger, J. de las Heras, G. Banerjee, E.J. Schwartz Source Type: research