HTA26 Portuguese Clinical Practice and Costs in the Treatment of Acid Sphingomyelinase Deficiency Disease

To describe the clinical practice and estimate the costs related to the treatment of acid sphingomyelinase deficiency disease (ASMD), type B or A/B, in the Portuguese National Health Service.

Source: Value in Health - December 1, 2023 Category: International Medicine & Public Health Authors: L. Silva Miguel, P. Carvalho, A. Oliveira, A. Guimas, E. Le ão Teles, S. Ferreira, C. Bulhosa, B. Pinheiro, M. Borges Source Type: research