Safety of Intravenous Administration of an AAV8 Vector Coding for an Oxidation-Resistant Human α1-Antitrypsin for the Treatment of α1-Antitrypsin Deficiency

Human Gene Therapy,Volume 34, Issue 3-4, Page 139-149, February 2023.

Source: Human Gene Therapy - February 14, 2023 Category: Genetics & Stem Cells Authors: Jonathan B. Rosenberg Bishnu P. De Alessandria Greco Nicholas Gorman Vikrum Kooner Alvin Chen Melissa Yost-Bido Carlos Munoz-Zuluaga Stephen M. Kaminsky Mahboubeh Rostami S ébastien Monette Ronald G. Crystal Dolan Sondhi Source Type: research