PPMD Sends Letter to FDA Regarding Duchenne Therapies
PPMD has sent a letter to the FDA requesting updates on various regulatory actions of tremendous importance to the Duchenne community. (Source: Parent Project Muscular Dystrophy)
Source: Parent Project Muscular Dystrophy - August 5, 2016 Category: Neurology Source Type: news
Help the Powers Family #TackleDuchenne!
The 9th Annual Coach To Cure MD on September 24 is shaping up to be our biggest year yet! Duchenne mom Kim Powers shares why this is the year you should get in the game and help us #TackleDuchenne. (Source: Parent Project Muscular Dystrophy)
Source: Parent Project Muscular Dystrophy - August 4, 2016 Category: Neurology Source Type: news
2016 Connect Conference Resources & Recordings
We are excited to share with you presentations from PPMD ’s 22nd Annual Connect Conference! We will continue to update this page over the coming weeks with slides and video content. (Source: Parent Project Muscular Dystrophy)
Source: Parent Project Muscular Dystrophy - July 26, 2016 Category: Neurology Source Type: news
[Webinar Recording] What is CRISPR/Cas9?
PPMD welcomed Dr. Eric Olson from UT Southwestern Medical Center to discuss the basics of gene editing and the potential permanent correction of Duchenne mutations with CRISPR/Cas9. (Source: Parent Project Muscular Dystrophy)
Source: Parent Project Muscular Dystrophy - July 20, 2016 Category: Neurology Source Type: news
[Upcoming Webinar - 7/13] What is CRISPR/Cas9?
PPMD welcomes Dr. Eric Olson from the Department of Molecular Biology at UT Southwestern Medical Center to discuss the basics of gene editing and the potential permanent correction of Duchenne mutations with CRISPR/Cas9. (Source: Parent Project Muscular Dystrophy)
Source: Parent Project Muscular Dystrophy - July 7, 2016 Category: Neurology Source Type: news
PPMD Receives Grant from Marathon Pharmaceuticals to Help Support Acclaimed Certified Duchenne Care Center Program
The grant will enable PPMD to provide additional resources to improve patient care and patient recruitment for clinical trials through the centers. (Source: Parent Project Muscular Dystrophy)
Source: Parent Project Muscular Dystrophy - July 7, 2016 Category: Neurology Source Type: news
Join the 2016 #PPMDConnect Conference Online!
Unable to attend this year's Annual Connect Conference in Orlando? Join us online! PPMD will be live streaming and our DuchenneConnect team will be live tweeting updates June 26-28. (Source: Parent Project Muscular Dystrophy)
Source: Parent Project Muscular Dystrophy - June 23, 2016 Category: Neurology Source Type: news
PPMD Awards The Ohio State University Grant to Support Cardiomyopathy Therapy for Duchenne
Heart issues don't just affect some people with Duchenne; they affect all people with Duchenne. PPMD is so grateful to the work being done at institutes like The Ohio State University and we are proud to support Dr. Guttridge. (Source: Parent Project Muscular Dystrophy)
Source: Parent Project Muscular Dystrophy - June 22, 2016 Category: Neurology Source Type: news
Understanding Gene Therapy & CRISPR/Cas9
Find out more about the latest in gene therapy, CRISPR/Cas9, and what these technologies could mean for Duchenne during three different opportunities this summer that promise to provide an in-depth analysis. < div class="feedflare" > < a href="http://feeds.parentprojectmd.org/~ff/ppmd?a=dEHOZG2-GYE:tnqV7-inTHs:yIl2AUoC8zA" > < img src="http://feeds.feedburner.com/~ff/ppmd?d=yIl2AUoC8zA" border="0" > < /img > < /a > < a href="http://feeds.parentprojectmd.org/~ff/ppmd?a=dEHOZG2-GYE:tnqV7-inTHs:qj6IDK7rITs" > < img src="http://feeds.feedburner.com/~ff/ppmd?d=qj6IDK7rITs" border="0" > < /img > < /a > < a href="http://feeds.par...
Source: Parent Project Muscular Dystrophy - June 20, 2016 Category: Neurology Source Type: news
Understanding Gene Therapy & CRISPR/Cas9
Find out more about the latest in gene therapy, CRISPR/Cas9, and what these technologies could mean for Duchenne during three different opportunities this summer that promise to provide an in-depth analysis. (Source: Parent Project Muscular Dystrophy)
Source: Parent Project Muscular Dystrophy - June 20, 2016 Category: Neurology Source Type: news
[Webinar Recording] MoveDMD: A Clinical Trial of Edasalonexent (CAT-1004) in Duchenne
PPMD and Dr. Joanne Donovan recently hosted a webinar to review information on edasalonexent (previously known as CAT-1004) and the MoveDMD trial. (Source: Parent Project Muscular Dystrophy)
Source: Parent Project Muscular Dystrophy - June 11, 2016 Category: Neurology Source Type: news
Getting Results: Success from your Advocacy efforts in February!
Your actions this year have yielded incredible results for Duchenne related funding at the federal level. (Source: Parent Project Muscular Dystrophy)
Source: Parent Project Muscular Dystrophy - June 10, 2016 Category: Neurology Source Type: news
PPMD Awards University of Washington Grant to Support Technology to Help Optimize Gene Therapy
PPMD is proud to support Dr. Odom from the University of Washington and we are hopeful that his work will help make gene therapy in Duchenne more effective and long lasting. (Source: Parent Project Muscular Dystrophy)
Source: Parent Project Muscular Dystrophy - June 9, 2016 Category: Neurology Source Type: news
PPMD & BIO Release New Report on the Development of Patient Preference Studies
PPMD hopes that this report will provide guidance for companies seeking to incorporate the patient perspective at every stage of developing and delivering innovative new treatments. < div class="feedflare" > < a href="http://feeds.parentprojectmd.org/~ff/ppmd?a=BfWi0Tue2Yk:QmJ1eXY4PyA:yIl2AUoC8zA" > < img src="http://feeds.feedburner.com/~ff/ppmd?d=yIl2AUoC8zA" border="0" > < /img > < /a > < a href="http://feeds.parentprojectmd.org/~ff/ppmd?a=BfWi0Tue2Yk:QmJ1eXY4PyA:qj6IDK7rITs" > < img src="http://feeds.feedburner.com/~ff/ppmd?d=qj6IDK7rITs" border="0" > < /img > < /a > < a href="http://feeds.parentprojectmd.org/~ff/ppmd?...
Source: Parent Project Muscular Dystrophy - June 8, 2016 Category: Neurology Source Type: news
PPMD & BIO Release New Report on the Development of Patient Preference Studies
PPMD hopes that this report will provide guidance for companies seeking to incorporate the patient perspective at every stage of developing and delivering innovative new treatments. (Source: Parent Project Muscular Dystrophy)
Source: Parent Project Muscular Dystrophy - June 8, 2016 Category: Neurology Source Type: news
