Generalized pairwise comparisons of prioritized outcomes are a powerful and patient-centric analysis of multi-domain scores

Generalized pairwise comparisons (GPC) can be used to assess the net benefit of new treatments for rare diseases. We show the potential of GPC through simulations based on data from a natural history study in ...

Source: Orphanet Journal of Rare Diseases - October 12, 2023 Category: Internal Medicine Authors: Vaiva Deltuvaite-Thomas, Micka ël De Backer, Samantha Parker, Marie Deneux, Lynda E. Polgreen, Cara O’Neill, Samuel Salvaggio and Marc Buyse Tags: Research Source Type: research